Wilson Disease
Watchlist
Retrieved
2021-01-23
Source
Trials
—
Genes
ATP7B,
ANXA5,
CP,
APOE,
PRNP,
IL6,
AHCY,
LOX,
TNF,
IL10,
LOXL2,
A2M,
SNCA,
NDUFB7,
PPP3CB,
PPP3CA,
CXCL8,
CAMK2A,
TIMP1,
HAMP,
ASMT,
SDHAF2,
BHMT,
ANKS1B,
ATP7A,
CYP27B1,
HMGCR,
SMPD1,
ESD,
ATOX1
ATP7B,
ANXA5,
CP,
APOE,
PRNP,
IL6,
AHCY,
LOX,
TNF,
IL10,
LOXL2,
A2M,
SNCA,
NDUFB7,
PPP3CB,
PPP3CA,
CXCL8,
CAMK2A,
TIMP1,
HAMP,
ASMT,
SDHAF2,
BHMT,
ANKS1B,
ATP7A,
CYP27B1,
HMGCR,
SMPD1,
ESD,
ATOX1,
COMMD1,
HFE,
MBD6,
ALB,
TP53,
SLC31A1,
GPT,
MBD1,
PANK2,
SERPINA1,
PNOC,
STON1,
IL1B,
GCH1,
GTF2A1L,
STON1-GTF2A1L,
AFM,
G6PD,
BDNF,
FXN,
ARSA,
GLUL,
BMS1,
SLC39A14,
TBC1D9,
FNDC3A,
PDCD10,
ATHS,
CCL27,
AHSA1,
CCS,
XPR1,
GRAP2,
CHMP2B,
PRC1,
AIMP2,
XRCC5,
BEST1,
VEGFA,
VCAM1,
TYR,
TXN,
RNF19A,
SLC17A5,
ATRNL1,
IGAN1,
ACACA,
CCDC115,
PNPLA3,
DNAJC5,
ASRGL1,
ALPP,
PAGR1,
SLC39A8,
CPAT1,
RBPJP4,
POLDIP2,
AMELX,
XIAP,
NAT10,
INO80,
IL23A,
GOLM1,
ZDHHC2,
PDLIM3,
CALCR,
BRAF,
CAT,
GALNS,
THRB,
MT1X,
ACE,
LTA,
DDIT3,
DMD,
KDR,
IDO1,
IL13,
DMRT1,
DNAH8,
DRD2,
IL2,
IL1RN,
IL1R1,
IL1A,
HNF4A,
FOXA2,
FOXA1,
GAST,
GRM5,
GPX1,
MTF1,
MTHFR,
SERPINA3,
MAPK8,
SPG7,
SOD2,
CFTR,
CLU,
SLPI,
RXRA,
RB1,
PROP1,
SLC31A2,
MAPK1,
DBH,
CRK,
CRP,
PPARG,
MAPK14,
CTNNB1,
ABCB1,
PAH,
OPA1,
SLC11A2,
NDUFAB1
Drugs
Adeno-associated viral vector serotype Anc80 containing the truncated human ATP7B gene under the control of the human alpha-1 antitrypsin promoter,
Ammonium tetrathiomolybdate,
Choline tetrathiomolybdate
Adeno-associated viral vector serotype Anc80 containing the truncated human ATP7B gene under the control of the human alpha-1 antitrypsin promoter,
Ammonium tetrathiomolybdate,
Choline tetrathiomolybdate,
Trientine dihydrochloride
(
CUFENCE,
METALITE,
SYPRINE
),
Zinc acetate
(
GALZIN,
WILZIN
),
adeno-associated viral vector serotype 8 encoding the human ATP7B gene under the control of the human alpha-1 antitrypsin promoter,
trientine tetrahydrochloride
(
CUPRIOR
)
Registered!